Fachrepositorium Lebenswissenschaften

4 Treffer

Kurzansicht	E-Jahr	Typ
JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam 2024 . Chiriboga, Claudia A. \| Bruno, Claudio \| Duong, Tina \| Fischer, Dirk \| Mercuri, Eugenio \| Kirschner, Janbernd \| Kostera-Pruszczyk, Anna \| Jaber, Birgit \| Gorni, Ksenija \| KLETZL, Heidemarie \| Carruthers, Imogen \| Martin, Carmen \| Scalco, Renata \| Fontoura, Paulo \| Muntoni, Francesco \| the JEWELFISH Study Group	2024	http://purl.org/ontology/bibo/Article
Risdiplam therapy in adults with 5q-SMA: observational study on motor function and treatment satisfaction 2024 . Bjelica, Bogdan \| Wohnrade, Camilla \| Cespedes, Iraima \| Osmanovic, Alma \| Schreiber-Katz, Olivia \| Petri, Susanne	2024	http://purl.org/ontology/bibo/Article
Risdiplam improves subjective swallowing quality in non-ambulatory adult patients with 5q-spinal muscular atrophy despite advanced motor impairment 2024 . Brakemeier, S. \| Lipka, J. \| Schlag, M. \| Kleinschnitz, C. \| Hagenacker, Tim	2024	http://purl.org/ontology/bibo/Article
Postnatal management of preterm infants with spinal muscular atrophy: experience from German newborn screening 2024 . Trollmann, Regina \| Johannsen, Jessika \| Vill, Katharina \| Köhler, Cornelia \| Hahn, Andreas \| Illsinger, Sabine \| Pechmann, Astrid \| Hagen, Maja von der \| Müller-Felber, Wolfgang	2024	http://purl.org/ontology/bibo/Article

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