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Sacherschließung
Young Adult [MeSH]
(2)
mTOR inhibitor therapy
(1)
article
(1)
Tuberous sclerosis complex
(1)
Severity of Illness Index [MeSH]
(1)
Scale for the assessment and rating of ataxia
(1)
Retrospective Studies [MeSH]
(1)
Research
(1)
Reproducibility of Results [MeSH]
(1)
Reference Values [MeSH]
(1)
Publikationstyp
Artikel
(3)
Medium
Erscheinungsjahr
2025
(1)
2024
(1)
2023
(1)
Institution
3 Treffer
Kurzansicht
E-Jahr
Zugriff
Typ
Operations
Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
2025 .
Driedger, Jan H.
|
Schröter, Julian
|
PROTECT-Study Group
|
Hertzberg, Christoph
|
Weschke, Bernhard
|
Kaindl, Angela M.
|
Lücke, Thomas
|
Thiels, Charlotte
|
Klotz, Kerstin Alexandra
|
Fazeli, Walid
|
Rostásy, Kevin
|
Wiethoff-Ubrig, Lucia
|
Kaiser, Olaf
|
Trollmann, Regina
|
Mammadova, Dilbar
|
Schubert-Bast, Susanne
|
Bach, Alexia
|
Eckenweiler, Matthias
|
Schönberger, Jan
|
Martakis, Kyriakos
|
Hahn, Andreas
|
Brockmann, Knut
|
Dreha-Kulaczewski, Steffi
|
Weiss, Deike
|
Denecke, Jonas
|
Muhle, Hiltrud
|
Arelin, Maria
|
Merkenschlager, Andreas
|
Borggräfe, Ingo
|
Roser, Timo
|
Ebrahimi-Fakhari, Daniel
|
Fiedler, Barbara
|
Schlump, Jan-Ulrich
|
Köster, Ilka
|
Korenke, Christoph
|
Alber, Michael
|
Ruf, Susanne
|
Feucht, Martha
|
Scholl, Theresa
|
Syrbe, Steffen
|
Saffari, Afshin
2025
http://purl.org/ontology/bibo/Article
Assessment of the reliability, responsiveness, and meaningfulness of the scale for the assessment and rating of ataxia (SARA) for lysosomal storage disorders
2024 .
Park, Julien H.
|
Bremova-Ertl, Tatiana
|
Brands, Marion
|
Foltan, Tomas
|
Gautschi, Matthias
|
Gissen, Paul
|
Hahn, Andreas
|
Jones, Simon
|
Arash-Kaps, Laila
|
Kolnikova, Miriam
|
Patterson, Marc
|
Perlman, Susan
|
Ramaswami, Uma
|
Reichmannová, Stella
|
Rohrbach, Marianne
|
Schneider, Susanne A.
|
Shaikh, Aasef
|
Sivananthan, Siyamini
|
Synofzik, Matthis
|
Walterfarng, Mark
|
Wibawa, Pierre
|
Martakis, Kyriakos
|
Manto, Mario
2024
http://purl.org/ontology/bibo/Article
Multivariable reference centiles for maximum grip strength in childhood to young adults
2023 .
Duran, Ibrahim
|
Wloka, Kim Ramona
|
Martakis, Kyriakos
|
Spiess, Karoline
|
Alexy, Ute
|
Schoenau, Eckhard
2023
http://purl.org/ontology/bibo/Article